http://randolab.stanford.edu/wp-content/uploads/2017/10/Rando-Lab-Logo-01-450x204.png 0 0 dpagano http://randolab.stanford.edu/wp-content/uploads/2017/10/Rando-Lab-Logo-01-450x204.png dpagano2005-12-26 18:34:232017-07-26 04:31:12Gene Therapy For Muscular Dystrophy Fixes Frail Muscle Cells In Animal Model, Stanford Study Finds
Gene Therapy For Muscular Dystrophy Fixes Frail Muscle Cells In Animal Model, Stanford Study Finds
STANFORD, Calif. — A new gene therapy technique that has shown promise in skin disease and hemophilia might one day be useful for treating muscular dystrophy, according to a new study by researchers at Stanford University School of Medicine.
In the study, published online in the Proceedings of the National Academy of Sciences the week of Jan. 2, the researchers used gene therapy to introduce a healthy copy of the gene dystrophin into mice with a condition that mimics muscular dystrophy. The dystrophin gene is mutated and as a result produces a defective protein in the roughly 20,000 people in the United States with the most common form of the disease.